Disease duration and survival in Brazilian Niemann-Pick disease type C patients: Preliminary data on potential impact of miglustat
| Autor: | Giugliani, Luciana, Van der Linder, Vanesa, Van Der Linden, Helio, Junior, Lourenço, Charles Marques, de Araújo Leão, Emília Katiane Embiruçu, Arita, Juliana Harumi, Doriqui, Maria Julia Rodovalho, Neto, Pedro Braga, de Souza, Carolina Fischinger Moura, Horovitz, Dafne Dain Gandelman, Santos, Mara Lucia, Grillo, Eugenio, da Silva, Raquel Tavares Boy, de Oliveira Abrão, Janaina Bianca, Trapp, Franciele Barbosa, Giugliani, Roberto |
|---|---|
| Zdroj: | In Molecular Genetics and Metabolism February 2016 117(2):S50-S51 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect