Histologic characterization of the progression of central nervous system pathology in the mucopolysaccharidosis IIIB (MPS IIIB, Sanfilippo syndrome type B) mouse model and bio-distribution and efficacy of the intracerebroventricular enzyme replacement therapy, BMN 250
| Autor: | Bagri, Anil, Harmon, Danielle, Vincelette, Jon, Vitelli, Catherine, Minto, Wesley, Yates, Bridget, Rigney, Sara, Santiago, Pam, Baridon, Brian, Xie, Lin, Gorostiza, Olivia, Christianson, Terri, Tiger, Pascale M.N., Yip, Bryan K., Lo, Melanie J., Holtzinger, John, Chen, Eric, Aoyagi-Scharber, Mika, Fitzpatrick, Paul, LeBowitz, Jonathan H., Bullens, Sherry, Bunting, Stuart |
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| Zdroj: | In Molecular Genetics and Metabolism February 2016 117(2):S23-S24 |
| Databáze: | ScienceDirect |
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