Intra-articular enzyme replacement therapy with rhIDUA is safe, well-tolerated, and reduces articular GAG storage in the canine model of mucopolysaccharidosis type I

Autor: Wang, Raymond Y., Aminian, Afshin, McEntee, Michael F., Kan, Shih-Hsin, Simonaro, Calogera M., Lamanna, William C., Lawrence, Roger, Ellinwood, N. Matthew, Guerra, Catalina, Le, Steven Q., Dickson, Patricia I., Esko, Jeffrey D.
Zdroj: In Molecular Genetics and Metabolism August 2014 112(4):286-293
Databáze: ScienceDirect