O7-6 Restoration of dystrophin in DMD: a single blind, placebo-controlled dose escalation study using Morpholino oligomer AVI-4658
| Autor: | Kinali, M., Arechavala-Gomeza, V., Feng, L., Cirak, S., Hunt, D., Adkin, C., Guglieri, M., Ashton, E., Rutherford, M., Mcculley, C., Popplewell, L., Graham, I.R., Wells, D.J., Wilton, S., Holt, T., Kole, R., Straub, V., Bushby, K., Sewry, C., Muntoni, F., Morgan, J.E., Nihoyannopoulos, P., Garralda, M.E., Abbs, S., Dickson, G., Wood, M.J.A. |
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| Zdroj: | In European Journal of Paediatric Neurology 2009 13 Supplement 1:S17-S17 |
| Databáze: | ScienceDirect |
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