Longitudinal Analysis of Ocular Disease in Children with Mucopolysaccharidosis I after Hematopoietic Cell Transplantation

Autor: van den Broek, Brigitte T.A., van Egmond-Ebbeling, Michelle B., Achterberg, Jens A., Boelens, Jaap Jan, Vlessert, Isa C., Prinsen, Hubertus C.M.T., van Doorn, Jaap, van Hasselt, Peter M.
Zdroj: In Biology of Blood and Marrow Transplantation May 2020 26(5):928-935
Databáze: ScienceDirect