Combined home enzyme replacement therapy and unrelated cord blood transplantation for Hurler’s syndrome (MPSI) in a pediatric HSCT center

Autor: Rodriguez, M., Khimji, I., Rhodd, S., Lapage, C., Zalesky, L., Jimenez, P., Barbouth, D., Elsas, L., Kleiner, G.
Zdroj: In Biology of Blood and Marrow Transplantation 2005 11(2) Supplement 1:97-97
Databáze: ScienceDirect