Spinal presentations in children with spinal muscular atrophy type 1 following gene therapy treatment with onasemnogene abeparvovec – The SMA REACH UK network experience
| Autor: | Wolfe, Amy, Sheehan, Jennie, Schofield, Alex, Cranney, Helen, O'Reilly, Emer, Stimpson, Georgia, Andrews, Alice, Vanegas, Maria, Lucas, Jonathan, Scoto, Mariacristina, Gowda, Vasantha, Wraige, Elizabeth, Jungbluth, Heinz |
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| Zdroj: | In Neuromuscular Disorders November 2024 44 |
| Databáze: | ScienceDirect |
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