P01 Risdiplam experience following onasemnogene abeparvovec in individuals with spinal muscular atrophy: a multicenter case series
| Autor: | Kuntz, N., Svoboda, M., Leon-Astudillo, C., Byrne, B., Krueger, J., Kwon, J., Sieburg, C., Castro, D. |
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| Zdroj: | In Neuromuscular Disorders October 2023 33 Supplement 1:S162-S162 |
| Databáze: | ScienceDirect |
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