P391 Phase 1 study to assess safety, tolerability, pharmacokinetics, and pharmacodynamics of PGN-EDODM1 in adults with myotonic dystrophy type 1 (DM1)

Autor: Shoskes, J., Larkindale, J., Cormier, J., Hand, H., Vacca, S., Lonkar, P., Holland, A., Garg, B., Foy, J., Mellion, M.
Zdroj: In Neuromuscular Disorders October 2023 33 Supplement 1:S156-S156
Databáze: ScienceDirect