P385 Development of an AAV-mediated Pentatricopeptide Repeat Protein (PPR) delivery system for treatment of myotonic dystrophy type 1 (DM1)
| Autor: | Imai, T., Miyai, M., Tamai, T., Ohta, M., Hada, K., Yagi, Y., Nakanishi, O., Mochizuki, H., Nakamori, M. |
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| Zdroj: | In Neuromuscular Disorders October 2023 33 Supplement 1:S154-S155 |
| Databáze: | ScienceDirect |
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