P68 Outcomes in patients with spinal muscular atrophy (SMA) and four or more SMN2 copies treated with onasemnogene abeparvovec: findings from RESTORE
| Autor: | Finkel, R., Benguerba, K., Gehani, M., Raju, D., Faulkner, E., LaMarca, N., Servais, L. |
|---|---|
| Zdroj: | In Neuromuscular Disorders October 2023 33 Supplement 1:S133-S133 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect