P28 The antisense oligonucleotide BMN 351 durably ameliorates dystrophic phenotypes in a mouse model of exon 51–skip-amenable Duchenne muscular dystrophy
| Autor: | Porco, D., Neil, D., Crawford, B., O'Neill, C., Qi, Y., Oppeneer, T., Larimore, K., Gupta, S., Beretta, F. |
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| Zdroj: | In Neuromuscular Disorders October 2023 33 Supplement 1:S104-S104 |
| Databáze: | ScienceDirect |
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