P.170 Safety, β-sarcoglycan expression, and functional outcomes from systemic gene transfer of bidridistrogene xeboparvovec in limb-girdle muscular dystrophy type 2E/R4
| Autor: | Rodino-Klapac, L., Pozsgai, E., Lewis, S., Griffin, D., Meadows, A., Lehman, K., Church, K., Reash, N., Iammarino, M., Sabo, B., Alfano, L., Lowes, L., Neuhaus, S., Li, X., Mendell, J. |
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| Zdroj: | In Neuromuscular Disorders October 2022 32 Supplement 1:S116-S116 |
| Databáze: | ScienceDirect |
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