FP.28 IGNITE DMD phase I/II study of SGT-001 microdystrophin gene therapy for DMD: Long-term outcomes and expression update

Autor: Dreghici, R. Donisa, Redican, S., Lawrence, J., Brown, K., Wang, F., Gonzalez, J., Schneider, J., Morris, C., Shieh, P., Byrne, B.
Zdroj: In Neuromuscular Disorders October 2022 32 Supplement 1:S98-S98
Databáze: ScienceDirect