P.110 JEWELFISH: 24-month safety and pharmacodynamic data in non-treatment-naïve patients with spinal muscular atrophy (SMA)
| Autor: | Chiriboga, C., Bruno, C., Duong, T., Fischer, D., Kirschner, J., Scoto, M., Mercuri, E., Gerber, M., Gorni, K., Kletzl, H., Carruthers, I., Martin, C., Gidaro, T., Muntoni, F. |
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| Zdroj: | In Neuromuscular Disorders October 2022 32 Supplement 1:S88-S88 |
| Databáze: | ScienceDirect |
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