Long-term effects of enzyme replacement therapy in an elderly cohort of late-onset Pompe disease

Autor: Winkler, Maren a, von Landenberg, Christina a, Kuchenbecker, Katharina a, Reimann, Jens a, Kornblum, Cornelia a, b, ⁎
Zdroj: In Neuromuscular Disorders March 2022 32(3):195-205
Databáze: ScienceDirect