DMD – ANIMAL MODELS & PRECLINICAL TREATMENT: P.220 Targeted genome editing in vivo corrects a Dmd duplication restoring wild-type dystrophin expression

Autor: Maino, E., Wojtal, D., Evagelou, S., Farheen, A., Wong, T., Lindsay, K., Scott, O., Chiodo, A., Schneeweiss, M., Rok, M., Ivakine, E., Cohn, R.
Zdroj: In Neuromuscular Disorders October 2020 30 Supplement 1:S110-S110
Databáze: ScienceDirect