DMD – BIOMARKERS & OUTCOME MEASURES: P.120 Phenotype and genotype characterization as predictors of DMD 45 to 55 multi-exon skipping therapy

Autor: Gargaun, E., Bassez, G., Wahbi, K., Yaou, R. Ben, Guibaud, M., Solé, G., Tiffreau, V., Laforet, P., Parent, M., Husson, M., Urtizberea, A., Eymard, B., Boland, A., Deleuze, J., Salgado, D., Khran, M., Levy, N., Blesius, A., Leturcq, F., Pietri-Rouxel, F.
Zdroj: In Neuromuscular Disorders October 2020 30 Supplement 1:S81-S81
Databáze: ScienceDirect