DMD TREATMENT: P.334PPMO pre-treatment is beneficial for AAV-based gene therapy in Duchenne muscular dystrophy

Autor: Forand, A., Muchir, A., Mougenot, N., Sevoz-Couche, C., Peccate, C., Lemaitre, M., Wood, M., Lorain, S., Piétri-Rouxel, F.
Zdroj: In Neuromuscular Disorders October 2019 29 Supplement 1:S164-S165
Databáze: ScienceDirect