P.178 - A phase 3 randomized, double blind, placebo-controlled study to evaluate the efficacy and safety of sialic acid extended-release tablets in patients with GNE myopathy (GNEM)

Autor: Lochmüller, H., Behin, A., Caraco, Y., Lau, H., Mirabella, M., Tournev, I., Tarnopolsky, M., Pogoryelova, O., Shah, J., Koutsoubos, T., Skrinar, A., Mansbach, H., Kakkis, E., Mozaffar, T.
Zdroj: In Neuromuscular Disorders October 2017 27 Supplement 2:S150-S150
Databáze: ScienceDirect