Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease

Autor: Case, Laura E., Bjartmar, Carl, Morgan, Claire, Casey, Robin, Charrow, Joel, Clancy, John P., Dasouki, Majed, DeArmey, Stephanie, Nedd, Khan, Nevins, Mary, Peters, Heidi, Phillips, Dawn, Spigelman, Zachary, Tifft, Cynthia, Kishnani, Priya S. *
Zdroj: In Neuromuscular Disorders April 2015 25(4):321-332
Databáze: ScienceDirect