P4.40 Enzyme Replacement Therapy and prognostic factors for response: An ongoing open-label cohort study in adults with Pompe Disease
| Autor: | de Vries, J.M., van der Beek, N.A.M., Hagemans, M.L.C., Hop, W.C.J., Reuser, A.J.J., van Doorn, P.A., van der Ploeg, A.T. |
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| Zdroj: | In Neuromuscular Disorders October 2011 21(9-10):716-716 |
| Databáze: | ScienceDirect |
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