Identification of pyrimidinyl piperazines as non-iminosugar glucocerebrosidase (GCase) pharmacological chaperones

Autor: Hoshikawa, Tamaki, Watanabe, Toru, Kotake, Makoto, Tiberghien, Nathalie, Woo, Chi-kit, Lewis, Sian, Briston, Thomas, Koglin, Mumta, Staddon, James M., Powney, Ben, Schapira, Anthony H.V., Takle, Andrew K.
Zdroj: In Bioorganic & Medicinal Chemistry Letters 1 February 2023 81
Databáze: ScienceDirect