Trofinetide Treatment Demonstrates a Benefit Over Placebo for the Ability to Communicate in Rett Syndrome

Autor: Neul, Jeffrey L., Percy, Alan K., Benke, Timothy A., Berry-Kravis, Elizabeth M., Glaze, Daniel G., Peters, Sarika U., Marsh, Eric D., An, Di, Bishop, Kathie M., Youakim, James M.
Zdroj: In Pediatric Neurology March 2024 152:63-72
Databáze: ScienceDirect