Efficacy and safety of givosiran for acute hepatic porphyria: Final results of the randomized phase III ENVISION trial

Autor: Kuter, David J., Bonkovsky, Herbert L., Monroy, Susana, Ross, Gayle, Guillén-Navarro, Encarna, Cappellini, Maria Domenica, Minder, Anna-Elisabeth, Hother-Nielsen, Ole, Ventura, Paolo, Jia, Gang, Sweetser, Marianne T., Thapar, Manish
Zdroj: In Journal of Hepatology November 2023 79(5):1150-1158
Databáze: ScienceDirect