PS-147 - ARO-AAT, a subcutaneous RNAi-based therapeutic for alpha-1 antitrypsin-related liver disease, demonstrates liver exposure-response and efficacy in preclinical studies

Autor: Wooddell, C., Blomenkamp, K., Chen, H., Griffin, J., Zhu, R., Chu, Q., Hamilton, H., Hegge, J., Christianson, D., Li, Z., Teckman, J., Given, B.
Zdroj: In Journal of Hepatology April 2018 68 Supplement 1:S82-S82
Databáze: ScienceDirect