Efficacy and safety of fitusiran prophylaxis in people with haemophilia A or haemophilia B with inhibitors (ATLAS-INH): a multicentre, open-label, randomised phase 3 trial
Autor: | Young, Guy *, Srivastava, Alok, Kavakli, Kaan, Ross, Cecil, Sathar, Jameela, You, Chur-Woo, Tran, Huyen, Sun, Jing, Wu, Runhui, Poloskey, Stacey, Qiu, Zhiying, Kichou, Salim, Andersson, Shauna, Mei, Baisong, Rangarajan, Savita |
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Zdroj: | In The Lancet 29 April-5 May 2023 401(10386):1427-1437 |
Databáze: | ScienceDirect |
Externí odkaz: |