Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in adults with non-transfusion dependent α-thalassaemia or β-thalassaemia: an open-label, multicentre, phase 2 study
| Autor: | Kuo, Kevin H M *, Layton, D Mark, Lal, Ashutosh, Al-Samkari, Hanny, Bhatia, Joy, Kosinski, Penelope A, Tong, Bo, Lynch, Megan, Uhlig, Katrin, Vichinsky, Elliott P |
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| Zdroj: | In The Lancet 13-19 August 2022 400(10351):493-501 |
| Databáze: | ScienceDirect |
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