Oral 9-cis retinoid for childhood blindness due to Leber congenital amaurosis caused by RPE65 or LRAT mutations: an open-label phase 1b trial
| Autor: | Koenekoop, Robert K, Sui, Ruifang, Sallum, Juliana, van den Born, L Ingeborgh, Ajlan, Radwan, Khan, Ayesha, den Hollander, Anneke I, Cremers, Frans P M, Mendola, Janine D, Bittner, Ava K, Dagnelie, Gislin, Schuchard, Ronald A, Saperstein, David A |
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| Zdroj: | In The Lancet 25-31 October 2014 384(9953):1513-1520 |
| Databáze: | ScienceDirect |
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