Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study
| Autor: | Levy, Harvey L, Milanowski, Andrzej, Chakrapani, Anupam, Cleary, Maureen, Lee, Philip, Trefz, Friedrich K, Whitley, Chester B, Feillet, François, Feigenbaum, Annette S, Bebchuk, Judith D, Christ-Schmidt, Heidi, Dorenbaum, Alex |
|---|---|
| Zdroj: | In The Lancet 2007 370(9586):504-510 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|