An open-label pilot study of losmapimod to evaluate the safety, tolerability, and changes in biomarker and clinical outcome assessments in participants with facioscapulohumeral muscular dystrophy type 1

Autor: Kools, Joost, Voermans, Nicol, Jiang, John G., Mitelman, Olga, Mellion, Michelle L., Ramana, Vivekananda, van Engelen, Baziel G.M.
Zdroj: In Journal of the Neurological Sciences 15 July 2024 462
Databáze: ScienceDirect