A Prospective Natural History Study of Mucopolysaccharidosis Type IIIA

Autor: Shapiro, Elsa G., Nestrasil, Igor, Delaney, Kathleen A., Rudser, Kyle, Kovac, Victor, Nair, Nitin, Richard, Charles W., III, Haslett, Patrick, Whitley, Chester B.
Zdroj: In The Journal of Pediatrics March 2016 170:278-287
Databáze: ScienceDirect