Intracerebroventricular gene therapy that delays neurological disease progression is associated with selective preservation of retinal ganglion cells in a canine model of CLN2 disease

Autor: Whiting, Rebecca E.H. a, Jensen, Cheryl A. a, Pearce, Jacqueline W. b, Gillespie, Lauren E. a, Bristow, Daniel E. c, Katz, Martin L. a, ∗
Zdroj: In Experimental Eye Research May 2016 146:276-282
Databáze: ScienceDirect