Second Generation Adeno-Associated Viral Vector Using a Novel Factor VIII Variant with Improved Secretion Achieves Higher Factor VIII Expression in Non-Human Primates

Autor: Nguyen, Giang N. *, Seleme, Maria C. *, Lindgren, Jonathan R. *, Henriksen, Allysen C. *, Muehlmatt, Amy *, McFadden, Melanie *, Smith, Geary R. *, Sabatino, Denise E.
Zdroj: In Blood 15 November 2022 140 Supplement 1:1902-1903
Databáze: ScienceDirect