Gene therapy for hemophilia B using CB 2679d-GT: a novel factor IX variant with higher potency than factor IX Padua

Autor: Nair, Nisha *, De Wolf, Dries *, Nguyen, Phuong Anh, Pham, Quang Hong, Samara-Kuko, Ermira, Landau, Jeff, Blouse, Grant E., Chuah, Marinee K. **, Vanden Driessche, Thierry *
Zdroj: In Blood 27 May 2021 137(21):2902-2906
Databáze: ScienceDirect