BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression

Autor: Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W.J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce *, Monahan, Paul E.
Zdroj: In Blood 11 February 2021 137(6):763-774
Databáze: ScienceDirect