Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/β2-microglobulin–/– repopulating mobilized human peripheral blood CD34+ cells

Autor: Brenner, Sebastian *, Whiting-Theobald, Narda L., Linton, Gilda F., Holmes, Kevin L., Anderson-Cohen, Mindy, Kelly, Patrick F., Vanin, Elio F., Pilon, André M., Bodine, David M., Horwitz, Mitchell E., Malech, Harry L.
Zdroj: In Blood 15 October 2003 102(8):2789-2797
Databáze: ScienceDirect