Therapeutic levels of fetal hemoglobin in erythroid progeny of β-thalassemic CD34+ cells after lentiviral vector-mediated gene transfer

Autor: Wilber, Andrew, Hargrove, Phillip W., Kim, Yoon-Sang, Riberdy, Janice M., Sankaran, Vijay G., Papanikolaou, Eleni, Georgomanoli, Maria, Anagnou, Nicholas P., Orkin, Stuart H., Nienhuis, Arthur W., Persons, Derek A.
Zdroj: In Blood 10 March 2011 117(10):2817-2826
Databáze: ScienceDirect