Editing aberrant splice sites efficiently restores β-globin expression in β-thalassemia
| Autor: | Xu, Shuqian, Luk, Kevin, Yao, Qiuming, Shen, Anne H., Zeng, Jing, Wu, Yuxuan, Luo, Hong-Yuan, Brendel, Christian, Pinello, Luca, Chui, David H.K., Wolfe, Scot A. *, Bauer, Daniel E. |
|---|---|
| Zdroj: | In Blood 23 May 2019 133(21):2255-2262 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|