CRISPR/Cas9 PIG-A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs

Autor: Shin, Tae-Hoon *, Baek, Eun Jung *, Corat, Marcus A.F., Chen, Shirley, Metais, Jean-Yves, AlJanahi, Aisha A., Zhou, Yifan, Donahue, Robert E., Yu, Kyung-Rok *, Dunbar, Cynthia E.
Zdroj: In Blood 6 June 2019 133(23):2542-2545
Databáze: ScienceDirect