Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy
| Autor: | Cox, Timothy M., Drelichman, Guillermo, Cravo, Renata, Balwani, Manisha, Burrow, Thomas Andrew, Martins, Ana Maria, Lukina, Elena, Rosenbloom, Barry, Goker-Alpan, Ozlem, Watman, Nora, El-Beshlawy, Amal, Kishnani, Priya S., Pedroso, Maria Lucia, Gaemers, Sebastiaan J.M., Tayag, Regina, Peterschmitt, M.Judith |
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| Zdroj: | In Blood 27 April 2017 129(17):2375-2383 |
| Databáze: | ScienceDirect |
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