Targeting FVIII expression to endothelial cells regenerates a releasable pool of FVIII and restores hemostasis in a mouse model of hemophilia A

Autor: Shi, Qizhen *, Fahs, Scot A., Kuether, Erin L., Cooley, Brian C., Weiler, Hartmut, Montgomery, Robert R.
Zdroj: In Blood 21 October 2010 116(16):3049-3057
Databáze: ScienceDirect