P1453: STABLE TRANSDUCTION OF FETAL HEMOGLOBIN IN PATIENTS WITH SICKLE CELL DISEASE IN THE PHASE 1/2 MOMENTUM STUDY OF ARU-1801 GENE THERAPY AND REDUCED INTENSITY CONDITIONING
Autor: | M. Grimley, M. Kent, M. Asnani, A. Shrestha, S. Felker, C. Lutzko, P. Arumugam, S. Witting, J. Knight-Madden, O. Niss, C. Quinn, C. Lo, C. Little, A. Dong, P. Malik |
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Jazyk: | angličtina |
Rok vydání: | 2022 |
Předmět: | |
Zdroj: | HemaSphere, Vol 6, Pp 1335-1336 (2022) |
Druh dokumentu: | article |
ISSN: | 2572-9241 00008486 |
DOI: | 10.1097/01.HS9.0000848668.22824.43 |
Databáze: | Directory of Open Access Journals |
Externí odkaz: |