P1453: STABLE TRANSDUCTION OF FETAL HEMOGLOBIN IN PATIENTS WITH SICKLE CELL DISEASE IN THE PHASE 1/2 MOMENTUM STUDY OF ARU-1801 GENE THERAPY AND REDUCED INTENSITY CONDITIONING

Autor: M. Grimley, M. Kent, M. Asnani, A. Shrestha, S. Felker, C. Lutzko, P. Arumugam, S. Witting, J. Knight-Madden, O. Niss, C. Quinn, C. Lo, C. Little, A. Dong, P. Malik
Jazyk: angličtina
Rok vydání: 2022
Předmět:
Zdroj: HemaSphere, Vol 6, Pp 1335-1336 (2022)
Druh dokumentu: article
ISSN: 2572-9241
00008486
DOI: 10.1097/01.HS9.0000848668.22824.43
Databáze: Directory of Open Access Journals