P173: Establishing preclinical efficacy for the first AAV gene therapy for GSD IX γ2 across stages of progressive liver disease
| Autor: | Rebecca Gibson, Jeong-A Lim, Su Jin Choi, Neha Jumani, Deeksha Bali, Sarah Young, William Jeck, Baodong Sun, Aravind Asokan, Priya Kishnani |
|---|---|
| Jazyk: | angličtina |
| Rok vydání: | 2023 |
| Předmět: | |
| Zdroj: | Genetics in Medicine Open, Vol 1, Iss 1, Pp 100202- (2023) |
| Druh dokumentu: | article |
| ISSN: | 2949-7744 |
| DOI: | 10.1016/j.gimo.2023.100202 |
| Databáze: | Directory of Open Access Journals |
| Externí odkaz: |
|