P012: Pegtibatinase, an investigational enzyme replacement therapy for the treatment of classical homocystinuria: Latest findings from the COMPOSE phase 1/2 trial
| Autor: | Can Ficicioglu, Jaya Ganesh, Wendy Smith, Melissa Lah, David Kudrow, Jalé Güner, Sharon McDermott, Sagar Vaidya, Liz Wilkening, Janet Thomas, Harvey Levy |
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| Jazyk: | angličtina |
| Rok vydání: | 2024 |
| Předmět: | |
| Zdroj: | Genetics in Medicine Open, Vol 2, Iss , Pp 100889- (2024) |
| Druh dokumentu: | article |
| ISSN: | 2949-7744 |
| DOI: | 10.1016/j.gimo.2024.100889 |
| Databáze: | Directory of Open Access Journals |
| Externí odkaz: |
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