3024 COMET post hoc analysis: efficacy of long-term avalglucosidase alfa in subgroups of patients with late-onset Pompe disease

Autor: Mark Roberts, Jordi Diaz-Manera, Antonio Toscano, Sabrina Sacconi, Mazen M Dimachkie, Nicole Armstrong, Robert Henderson, Benedikt Schoser, Priya S Kishnani, Olivier Huynh-Ba, Nathan Thibault, Young Chul Choi, Shugo Suwazono, Paulo Victor Sgobbi de Souza, Magali Periquet
Jazyk: angličtina
Rok vydání: 2024
Předmět:
Zdroj: BMJ Neurology Open, Vol 6, Iss Suppl 1 (2024)
Druh dokumentu: article
ISSN: 2632-6140
DOI: 10.1136/bmjno-2024-ANZAN.49
Databáze: Directory of Open Access Journals