3024 COMET post hoc analysis: efficacy of long-term avalglucosidase alfa in subgroups of patients with late-onset Pompe disease
| Autor: | Mark Roberts, Jordi Diaz-Manera, Antonio Toscano, Sabrina Sacconi, Mazen M Dimachkie, Nicole Armstrong, Robert Henderson, Benedikt Schoser, Priya S Kishnani, Olivier Huynh-Ba, Nathan Thibault, Young Chul Choi, Shugo Suwazono, Paulo Victor Sgobbi de Souza, Magali Periquet |
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| Jazyk: | angličtina |
| Rok vydání: | 2024 |
| Předmět: | |
| Zdroj: | BMJ Neurology Open, Vol 6, Iss Suppl 1 (2024) |
| Druh dokumentu: | article |
| ISSN: | 2632-6140 |
| DOI: | 10.1136/bmjno-2024-ANZAN.49 |
| Databáze: | Directory of Open Access Journals |
| Externí odkaz: |
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