P1501: FOLLOW-UP RESULTS OF A PHASE 2 STUDY ASSESSING THE SAFETY AND EFFICACY OF MITAPIVAT TREATMENT, AN ORAL PYRUVATE KINASE ACTIVATOR, FOR UP TO 60 WEEKS IN SUBJECTS WITH SICKLE CELL DISEASE

Autor: M. J. van Dijk, M. A. Rab, B. A. van Oirschot, J. Bos, C. Derichs, A. W. Rijneveld, M. H. Cnossen, E. Nur, B. J. Biemond, M. Bartels, J. J. Jans, W. W. van Solinge, R. E. Schutgens, R. van Wijk, E. J. van Beers
Jazyk: angličtina
Rok vydání: 2022
Předmět:
Zdroj: HemaSphere, Vol 6, Pp 1382-1383 (2022)
Druh dokumentu: article
ISSN: 2572-9241
DOI: 10.1097/01.HS9.0000848860.58516.71
Databáze: Directory of Open Access Journals