Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase

Autor:	Harmatz, P, Giugliani, R, Schwartz, Iv, Guffon, N, Teles, El, Miranda, Mc, Wraith, Je, Beck, M, Arash, L, Scarpa, M, Ketteridge, D, Hopwood, Jj, Plecko, B, Steiner, R, Whitley, Cb, Kaplan, P, Yu, Zf, Swiedler, Sj, Decker, C, Barone, R, Fiumara, A, Pavone, L, Sorge, G, MPS VI STUDY GROUP
Jazyk:	angličtina
Rok vydání:	2008
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=od______4731::235fa8a0b6f968209cb9782a1e623045 http://hdl.handle.net/20.500.11769/50049 Zobrazit plný text záznamu