Advances in the Therapy of Spinal Muscular Atrophy
| Autor: | Jenna Klotz, John W. Day, Jacinda B. Sampson, MyMy C. Buu, Sally Dunaway Young, Carolina Tesi Rocha, Tina Duong |
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| Rok vydání: | 2021 |
| Předmět: |
Adult
Pathology medicine.medical_specialty Adolescent Recombinant Fusion Proteins Oligonucleotides Spinal Muscular Atrophies of Childhood medicine.disease_cause Young Adult medicine Humans Child Adeno-associated virus Biological Products medicine.diagnostic_test Lumbar puncture business.industry Gene replacement therapy Infant Newborn Infant Spinal muscular atrophy medicine.disease SMA Pyrimidines Neuromuscular Agents Child Preschool Pediatrics Perinatology and Child Health Nusinersen business Azo Compounds |
| Zdroj: | The Journal of pediatrics. 236 |
| ISSN: | 1097-6833 |
| Databáze: | OpenAIRE |
| Externí odkaz: |
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