miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3
Autor: | Rui Jorge Nobre, Diana D. Lobo, Carina Henriques, Sonia P. Duarte, Sara M. Lopes, Ana C. Silva, Miguel M. Lopes, Fanny Mariet, Lukas K. Schwarz, M.S. Baatje, Valerie Ferreira, Astrid Vallès, Luis Pereira de Almeida, Melvin M. Evers, Lodewijk J.A. Toonen |
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Rok vydání: | 2022 |
Předmět: | |
Zdroj: | Nucleic Acid Therapeutics. 32:194-205 |
ISSN: | 2159-3345 2159-3337 |
Popis: | Spinocerebellar ataxia type 3 (SCA3) is a neurodegenerative disorder caused by the expansion of a CAG repeat in the |
Databáze: | OpenAIRE |
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